Rare Disease Therapeutics
Part of Biotech - Drug Development
| Ticker | Company | Mkt Cap▼ | Price | Chg% | Volume |
|---|---|---|---|---|---|
 AMGN | Amgen Inc | $181.8b | $349.61 | +1.2% | 3.5M |
 VRTX | Vertex Pharmaceuticals Inc | $113.6b | $446.93 | +1.2% | 1.5M |
 ALNY | Alnylam Pharmaceuticals, Inc. | $40.3b | $303.03 | -0.2% | 1.0M |
 UTHR | United Therapeutics Corp | $23.6b | $549.59 | +0.3% | 663.2K |
 INSM | Insmed, Inc. | $23.2b | $94.15 | -10.3% | 8.0M |
 INCY | Incyte Genomics Inc | $19.3b | $102.39 | +1.1% | 2.6M |
 BBIO | BridgeBio Pharma, Inc. Common Stock | $13.0b | $67.61 | +0.4% | 2.6M |
 IONS | Ionis Pharmaceuticals, Inc. Common Stock | $12.6b | $74.49 | -0.9% | 2.0M |
 BMRN | BioMarin Pharmaceuticals Inc | $11.1b | $56.76 | +0.5% | 2.2M |
 ARWR | Arrowhead Research Corporation | $11.0b | $73.09 | -2.8% | 1.2M |
 CYTK | Cytokinetics Inc. | $10.4b | $71.44 | -1.2% | 1.6M |
 KRYS | Krystal Biotech, Inc. Common Stock | $9.1b | $300.46 | -2.4% | 264.5K |
 CORT | Corcept Therapeutics Inc. | $7.5b | $72.63 | -3.0% | 774.7K |
 MIRM | Mirum Pharmaceuticals, Inc. Common Stock | $6.2b | $93.43 | +1.0% | 585.3K |
 PTCT | PTC Therapeutics, Inc. | $6.1b | $70.94 | +0.4% | 937.1K |
 RYTM | Rhythm Pharmaceuticals, Inc. Common Stock | $6.1b | $86.42 | -1.4% | 446.3K |
 COGT | Cogent Biosciences, Inc. Common Stock | $6.0b | $31.00 | -5.5% | 1.8M |
 SRRK | Scholar Rock Holding Corporation Common Stock | $5.9b | $44.28 | -2.3% | 1.2M |
 LQDA | Liquidia Corporation Common Stock | $5.5b | $61.78 | -1.2% | 1.7M |
 CRSP | CRISPR Therapeutics AG | $5.4b | $51.86 | -8.9% | 2.3M |
 APLS | Apellis Pharmaceuticals, Inc. Common Stock | $5.2b | $41.04 | +0.0% | 68.6M |
 FOLD | Amicus Therapeutics, Inc | $4.5b | $14.49 | +0.0% | 3.5M |
 TVTX | Travere Therapeutics, Inc. Common Stock | $4.4b | $45.78 | -0.9% | 2.9M |
 CPRX | Catalyst Pharmaceutical Inc. | $3.8b | $31.28 | -0.0% | 1.5M |
 CRNX | Crinetics Pharmaceuticals, Inc. | $3.7b | $32.91 | -5.0% | 863.2K |
 EWTX | Edgewise Therapeutics, Inc. Common Stock | $3.7b | $35.55 | -4.5% | 3.0M |
 BEAM | Beam Therapeutics Inc. Common Stock | $3.4b | $29.34 | -10.7% | 2.4M |
 DYN | Dyne Therapeutics, Inc. Common Stock | $3.2b | $17.05 | -7.4% | 1.9M |
 SLNO | Soleno Therapeutics, Inc. Common Stock | $2.7b | $53.02 | +0.0% | 1.6M |
 IRON | Disc Medicine, Inc. Common Stock | $2.7b | $66.94 | -5.9% | 454.5K |
 TARS | Tarsus Pharmaceuticals, Inc. Common Stock | $2.6b | $59.28 | -1.8% | 370.1K |
 RARE | Ultragenyx Pharmaceutical Inc. | $2.4b | $21.92 | -6.0% | 1.1M |
 BCRX | BioCryst Pharmaceuticals Inc | $2.3b | $8.40 | -0.8% | 2.5M |
 PHVS | Pharvaris N.V. Ordinary Shares | $2.1b | $31.16 | -1.5% | 775.1K |
 OCUL | Ocular Therapeutix, Inc. | $2.0b | $8.26 | -6.1% | 1.3M |
 AUPH | Aurinia Pharmaceuticals Inc | $2.0b | $15.82 | -3.4% | 1.3M |
 NTLA | Intellia Therapeutics, Inc | $2.0b | $13.30 | -9.8% | 7.5M |
 VRDN | Viridian Therapeutics, Inc. Common Stock | $1.9b | $15.79 | -4.7% | 1.8M |
 SION | Sionna Therapeutics, Inc. Common Stock | $1.9b | $35.30 | -6.6% | 461.3K |
 STOK | Stoke Therapeutics, Inc. Common Stock | $1.9b | $30.04 | -0.3% | 569.5K |
 SRPT | Sarepta Therapeutics,, Inc. Common Stock | $1.9b | $15.75 | -5.5% | 2.7M |
 HRMY | Harmony Biosciences Holdings, Inc. Common Stock | $1.8b | $32.19 | -2.3% | 462.3K |
 QURE | uniQure N.V. | $1.8b | $26.54 | -5.2% | 1.5M |
 ANIP | ANI Pharmaceuticals, Inc. | $1.8b | $81.09 | +2.4% | 338.2K |
 AGIO | Agios Pharmaceuticals, Inc. | $1.7b | $28.31 | -1.7% | 561.3K |
 CAPR | Capricor Therapeutics Inc | $1.7b | $26.71 | -4.4% | 578.2K |
 PVLA | Palvella Therapeutics, Inc. Common Stock | $1.7b | $108.69 | -5.3% | 374.2K |
 TSHA | Taysha Gene Therapies, Inc. Common Stock | $1.7b | $5.50 | -6.6% | 1.4M |
 AMLX | Amylyx Pharmaceuticals, Inc. Common Stock | $1.6b | $13.30 | -7.1% | 1.7M |
 DMRA | Damora Therapeutics, Inc. Common Stock | $1.5b | $21.09 | -5.5% | 523.5K |