Rare Disease Therapeutics
Part of Biotech - Drug Development
| Ticker | Company | Mkt Cap▼ | Price | Chg% | Volume |
|---|---|---|---|---|---|
 AMGN | Amgen Inc | $188.1b | $344.51 | -1.0% | 574.6K |
 VRTX | Vertex Pharmaceuticals Inc | $112.6b | $439.54 | +0.2% | 148.6K |
 ALNY | Alnylam Pharmaceuticals, Inc. | $41.9b | $331.94 | +4.1% | 435.9K |
 INSM | Insmed, Inc. | $33.0b | $164.48 | +1.3% | 349.2K |
 UTHR | United Therapeutics Corp | $25.8b | $559.91 | -0.9% | 146.6K |
 INCY | Incyte Genomics Inc | $18.0b | $95.65 | -0.3% | 120.1K |
 BBIO | BridgeBio Pharma, Inc. Common Stock | $13.4b | $73.33 | +0.3% | 94.7K |
 IONS | Ionis Pharmaceuticals, Inc. Common Stock | $12.0b | $74.83 | +0.0% | 203.1K |
 BMRN | BioMarin Pharmaceuticals Inc | $10.5b | $55.93 | +0.8% | 283.6K |
 ARWR | Arrowhead Research Corporation | $8.1b | $61.69 | +1.1% | 251.4K |
 CYTK | Cytokinetics Inc. | $7.8b | $65.72 | -1.5% | 301.2K |
 KRYS | Krystal Biotech, Inc. Common Stock | $7.2b | $265.37 | +1.7% | 141.4K |
 COGT | Cogent Biosciences, Inc. Common Stock | $5.7b | $35.33 | +0.3% | 214.6K |
 PTCT | PTC Therapeutics, Inc. | $5.4b | $69.78 | +3.0% | 135.5K |
 MIRM | Mirum Pharmaceuticals, Inc. Common Stock | $5.3b | $96.22 | +2.2% | 75.5K |
 RYTM | Rhythm Pharmaceuticals, Inc. Common Stock | $5.3b | $88.18 | +2.2% | 214.5K |
 SRRK | Scholar Rock Holding Corporation Common Stock | $4.9b | $50.05 | +0.1% | 345.1K |
 FOLD | Amicus Therapeutics, Inc | $4.5b | $14.45 | +0.0% | 269.4K |
 CRSP | CRISPR Therapeutics AG | $4.3b | $49.99 | +1.0% | 245.7K |
 CORT | Corcept Therapeutics Inc. | $4.1b | $42.42 | -0.2% | 204.7K |
 CRNX | Crinetics Pharmaceuticals, Inc. | $3.6b | $38.49 | +3.4% | 160.5K |
 EWTX | Edgewise Therapeutics, Inc. Common Stock | $3.2b | $33.34 | +0.0% | 115.2K |
 LQDA | Liquidia Corporation Common Stock | $3.1b | $38.35 | +1.8% | 409.3K |
 CPRX | Catalyst Pharmaceutical Inc. | $2.9b | $24.80 | +0.5% | 132.8K |
 TARS | Tarsus Pharmaceuticals, Inc. Common Stock | $2.8b | $71.34 | +1.7% | 181.6K |
 DYN | Dyne Therapeutics, Inc. Common Stock | $2.8b | $18.70 | -0.8% | 346.5K |
 TVTX | Travere Therapeutics, Inc. Common Stock | $2.6b | $32.67 | +7.3% | 939.7K |
 BCRX | BioCryst Pharmaceuticals Inc | $2.4b | $9.46 | +4.8% | 776.3K |
 IRON | Disc Medicine, Inc. Common Stock | $2.3b | $65.19 | +0.0% | 39.5K |
 BEAM | Beam Therapeutics Inc. Common Stock | $2.2b | $24.87 | +0.9% | 359.8K |
 APLS | Apellis Pharmaceuticals, Inc. Common Stock | $2.2b | $40.58 | +0.4% | 2.5M |
 SRPT | Sarepta Therapeutics,, Inc. Common Stock | $2.2b | $23.17 | -0.3% | 564.9K |
 RARE | Ultragenyx Pharmaceutical Inc. | $1.9b | $22.68 | +1.0% | 296.3K |
 VRDN | Viridian Therapeutics, Inc. Common Stock | $1.9b | $13.75 | -27.0% | 6.4M |
 STOK | Stoke Therapeutics, Inc. Common Stock | $1.9b | $32.83 | +0.3% | 129.2K |
 AUPH | Aurinia Pharmaceuticals Inc | $1.9b | $15.98 | +2.4% | 412.3K |
 PHVS | Pharvaris N.V. Ordinary Shares | $1.8b | $28.36 | -0.7% | 23.8K |
 AGIO | Agios Pharmaceuticals, Inc. | $1.7b | $35.80 | +1.7% | 231.7K |
 ANIP | ANI Pharmaceuticals, Inc. | $1.7b | $76.56 | +3.2% | 137.3K |
 SION | Sionna Therapeutics, Inc. Common Stock | $1.6b | $39.51 | -2.4% | 33.9K |
 OCUL | Ocular Therapeutix, Inc. | $1.6b | $8.37 | -1.4% | 720.6K |
 CAPR | Capricor Therapeutics Inc | $1.6b | $33.23 | +3.5% | 195.1K |
 PVLA | Palvella Therapeutics, Inc. Common Stock | $1.6b | $124.18 | +0.6% | 45.7K |
 SLNO | Soleno Therapeutics, Inc. Common Stock | $1.6b | $52.22 | +32.2% | 43.4M |
 HRMY | Harmony Biosciences Holdings, Inc. Common Stock | $1.6b | $27.71 | -0.1% | 249.0K |
 DMRA | Damora Therapeutics, Inc. Common Stock | $1.5b | $25.22 | +0.5% | 48.1K |
 OCS | Oculis Holding AG Ordinary shares | $1.4b | $26.34 | -1.1% | 26.5K |
 AMLX | Amylyx Pharmaceuticals, Inc. Common Stock | $1.4b | $15.71 | +5.0% | 423.1K |
 NTLA | Intellia Therapeutics, Inc | $1.4b | $13.54 | +3.1% | 671.6K |
 ARDX | Ardelyx, Inc. | $1.4b | $6.05 | +1.9% | 421.6K |