Rare Disease Therapeutics
Part of Biotech - Drug Development
| Ticker | Company | Mkt Cap▼ | Price | Chg% | Volume |
|---|---|---|---|---|---|
 AMGN | Amgen Inc | $188.1b | $340.17 | -1.3% | 2.6M |
 VRTX | Vertex Pharmaceuticals Inc | $112.6b | $425.98 | -1.0% | 966.9K |
 ALNY | Alnylam Pharmaceuticals, Inc. | $41.9b | $308.65 | +1.0% | 1.1M |
 INSM | Insmed, Inc. | $33.0b | $136.00 | +0.6% | 1.1M |
 UTHR | United Therapeutics Corp | $25.8b | $567.16 | 0.0% | 242.4K |
 INCY | Incyte Genomics Inc | $18.0b | $95.70 | +1.1% | 2.1M |
 BBIO | BridgeBio Pharma, Inc. Common Stock | $13.4b | $74.49 | +1.7% | 3.0M |
 IONS | Ionis Pharmaceuticals, Inc. Common Stock | $12.0b | $72.28 | -1.3% | 2.3M |
 BMRN | BioMarin Pharmaceuticals Inc | $10.5b | $53.81 | +1.2% | 1.5M |
 ARWR | Arrowhead Research Corporation | $8.1b | $73.56 | -0.5% | 1.4M |
 CYTK | Cytokinetics Inc. | $7.8b | $61.63 | -5.7% | 2.3M |
 KRYS | Krystal Biotech, Inc. Common Stock | $7.2b | $272.65 | +0.0% | 242.4K |
 COGT | Cogent Biosciences, Inc. Common Stock | $5.7b | $36.60 | -0.6% | 1.0M |
 PTCT | PTC Therapeutics, Inc. | $5.4b | $69.23 | +1.5% | 1.1M |
 MIRM | Mirum Pharmaceuticals, Inc. Common Stock | $5.3b | $92.43 | +1.0% | 430.3K |
 RYTM | Rhythm Pharmaceuticals, Inc. Common Stock | $5.3b | $85.18 | -0.6% | 355.9K |
 SRRK | Scholar Rock Holding Corporation Common Stock | $4.9b | $46.27 | -0.5% | 1.3M |
 FOLD | Amicus Therapeutics, Inc | $4.5b | $14.49 | +0.0% | 5.3M |
 CRSP | CRISPR Therapeutics AG | $4.3b | $50.98 | +4.5% | 2.9M |
 CORT | Corcept Therapeutics Inc. | $4.1b | $46.20 | +0.3% | 646.7K |
 CRNX | Crinetics Pharmaceuticals, Inc. | $3.6b | $38.63 | +0.8% | 907.0K |
 EWTX | Edgewise Therapeutics, Inc. Common Stock | $3.2b | $30.64 | -3.0% | 1.1M |
 LQDA | Liquidia Corporation Common Stock | $3.1b | $37.35 | +0.1% | 791.3K |
 CPRX | Catalyst Pharmaceutical Inc. | $2.9b | $29.27 | +6.9% | 9.3M |
 TARS | Tarsus Pharmaceuticals, Inc. Common Stock | $2.8b | $60.97 | -0.8% | 563.8K |
 DYN | Dyne Therapeutics, Inc. Common Stock | $2.8b | $18.04 | -1.2% | 1.7M |
 TVTX | Travere Therapeutics, Inc. Common Stock | $2.6b | $40.84 | +0.8% | 1.0M |
 BCRX | BioCryst Pharmaceuticals Inc | $2.4b | $8.91 | -0.3% | 3.1M |
 IRON | Disc Medicine, Inc. Common Stock | $2.3b | $68.82 | -0.0% | 238.7K |
 BEAM | Beam Therapeutics Inc. Common Stock | $2.2b | $29.16 | +7.6% | 3.2M |
 APLS | Apellis Pharmaceuticals, Inc. Common Stock | $2.2b | $40.95 | +0.0% | 2.7M |
 SRPT | Sarepta Therapeutics,, Inc. Common Stock | $2.2b | $20.98 | +3.4% | 3.1M |
 RARE | Ultragenyx Pharmaceutical Inc. | $1.9b | $24.00 | -0.4% | 1.8M |
 VRDN | Viridian Therapeutics, Inc. Common Stock | $1.9b | $13.51 | -1.6% | 2.3M |
 STOK | Stoke Therapeutics, Inc. Common Stock | $1.9b | $33.74 | -0.8% | 276.0K |
 AUPH | Aurinia Pharmaceuticals Inc | $1.9b | $16.38 | +2.5% | 1.1M |
 PHVS | Pharvaris N.V. Ordinary Shares | $1.8b | $28.76 | +0.5% | 172.3K |
 AGIO | Agios Pharmaceuticals, Inc. | $1.7b | $24.44 | -3.5% | 1.1M |
 ANIP | ANI Pharmaceuticals, Inc. | $1.7b | $79.56 | +1.2% | 245.3K |
 SION | Sionna Therapeutics, Inc. Common Stock | $1.6b | $39.23 | +2.9% | 623.7K |
 OCUL | Ocular Therapeutix, Inc. | $1.6b | $9.52 | +0.3% | 2.5M |
 CAPR | Capricor Therapeutics Inc | $1.6b | $35.09 | -0.5% | 993.7K |
 PVLA | Palvella Therapeutics, Inc. Common Stock | $1.6b | $128.68 | +4.1% | 215.7K |
 SLNO | Soleno Therapeutics, Inc. Common Stock | $1.6b | $52.76 | +0.1% | 1.2M |
 HRMY | Harmony Biosciences Holdings, Inc. Common Stock | $1.6b | $31.05 | +0.8% | 831.9K |
 DMRA | Damora Therapeutics, Inc. Common Stock | $1.5b | $25.56 | +3.3% | 267.3K |
 OCS | Oculis Holding AG Ordinary shares | $1.4b | $27.10 | +2.5% | 616.3K |
 AMLX | Amylyx Pharmaceuticals, Inc. Common Stock | $1.4b | $16.86 | -1.1% | 859.2K |
 NTLA | Intellia Therapeutics, Inc | $1.4b | $13.03 | -4.4% | 27.1M |
 ARDX | Ardelyx, Inc. | $1.4b | $6.00 | +0.8% | 2.7M |