Rare Disease Therapeutics
Part of Biotech - Drug Development
| Ticker | Company | Mkt Cap▼ | Price | Chg% | Volume |
|---|---|---|---|---|---|
 AMGN | Amgen Inc | $183.1b | $323.88 | -0.7% | 802.1K |
 VRTX | Vertex Pharmaceuticals Inc | $109.4b | $439.16 | +0.5% | 685.7K |
 ALNY | Alnylam Pharmaceuticals, Inc. | $40.3b | $287.70 | +0.2% | 350.6K |
 INSM | Insmed, Inc. | $29.1b | $105.63 | -3.2% | 1.8M |
 UTHR | United Therapeutics Corp | $24.9b | $566.15 | -0.4% | 106.8K |
 INCY | Incyte Genomics Inc | $19.5b | $95.25 | -0.1% | 402.6K |
 BBIO | BridgeBio Pharma, Inc. Common Stock | $13.5b | $64.31 | -2.7% | 1.7M |
 IONS | Ionis Pharmaceuticals, Inc. Common Stock | $11.9b | $72.28 | -2.6% | 1.2M |
 BMRN | BioMarin Pharmaceuticals Inc | $10.3b | $49.81 | -3.9% | 1.9M |
 ARWR | Arrowhead Research Corporation | $9.8b | $74.30 | -3.1% | 748.9K |
 KRYS | Krystal Biotech, Inc. Common Stock | $7.9b | $293.46 | -4.2% | 125.7K |
 CYTK | Cytokinetics Inc. | $7.5b | $75.91 | +0.1% | 670.5K |
 COGT | Cogent Biosciences, Inc. Common Stock | $6.2b | $31.75 | -2.9% | 721.4K |
 PTCT | PTC Therapeutics, Inc. | $5.8b | $70.19 | -1.8% | 370.6K |
 RYTM | Rhythm Pharmaceuticals, Inc. Common Stock | $5.7b | $87.00 | -3.9% | 288.3K |
 MIRM | Mirum Pharmaceuticals, Inc. Common Stock | $5.7b | $95.56 | -6.5% | 432.6K |
 SRRK | Scholar Rock Holding Corporation Common Stock | $5.6b | $47.10 | -4.6% | 359.3K |
 APLS | Apellis Pharmaceuticals, Inc. Common Stock | $5.2b | $41.04 | +0.0% | 68.6M |
 CRSP | CRISPR Therapeutics AG | $5.0b | $48.60 | +0.4% | 895.2K |
 CORT | Corcept Therapeutics Inc. | $5.0b | $55.80 | -1.0% | 315.1K |
 FOLD | Amicus Therapeutics, Inc | $4.5b | $14.49 | +0.0% | 3.5M |
 CRNX | Crinetics Pharmaceuticals, Inc. | $4.0b | $35.10 | -4.5% | 276.9K |
 TVTX | Travere Therapeutics, Inc. Common Stock | $3.8b | $43.05 | +1.1% | 653.5K |
 CPRX | Catalyst Pharmaceutical Inc. | $3.6b | $31.22 | +0.1% | 2.2M |
 LQDA | Liquidia Corporation Common Stock | $3.3b | $56.36 | -1.0% | 773.6K |
 EWTX | Edgewise Therapeutics, Inc. Common Stock | $3.3b | $31.93 | -3.5% | 337.7K |
 BEAM | Beam Therapeutics Inc. Common Stock | $3.1b | $27.13 | -2.9% | 829.9K |
 DYN | Dyne Therapeutics, Inc. Common Stock | $3.0b | $16.70 | -3.4% | 659.6K |
 SLNO | Soleno Therapeutics, Inc. Common Stock | $2.7b | $53.02 | +0.0% | 1.6M |
 TARS | Tarsus Pharmaceuticals, Inc. Common Stock | $2.6b | $63.41 | +1.5% | 223.9K |
 IRON | Disc Medicine, Inc. Common Stock | $2.6b | $66.76 | -0.1% | 241.0K |
 RARE | Ultragenyx Pharmaceutical Inc. | $2.4b | $24.34 | -2.7% | 445.7K |
 BCRX | BioCryst Pharmaceuticals Inc | $2.3b | $9.03 | +0.1% | 1.5M |
 SRPT | Sarepta Therapeutics,, Inc. Common Stock | $2.2b | $17.08 | -2.7% | 1.2M |
 AUPH | Aurinia Pharmaceuticals Inc | $2.1b | $15.57 | +1.9% | 598.5K |
 OCUL | Ocular Therapeutix, Inc. | $2.0b | $8.60 | -6.2% | 1.2M |
 STOK | Stoke Therapeutics, Inc. Common Stock | $2.0b | $28.95 | -3.7% | 238.5K |
 CAPR | Capricor Therapeutics Inc | $2.0b | $27.85 | -3.3% | 422.9K |
 PHVS | Pharvaris N.V. Ordinary Shares | $1.8b | $29.18 | -4.0% | 193.5K |
 AMLX | Amylyx Pharmaceuticals, Inc. Common Stock | $1.8b | $12.83 | -3.4% | 536.9K |
 TSHA | Taysha Gene Therapies, Inc. Common Stock | $1.8b | $5.50 | -7.8% | 1.1M |
 HRMY | Harmony Biosciences Holdings, Inc. Common Stock | $1.8b | $29.84 | -0.8% | 227.5K |
 PVLA | Palvella Therapeutics, Inc. Common Stock | $1.8b | $105.63 | -7.5% | 155.2K |
 SION | Sionna Therapeutics, Inc. Common Stock | $1.8b | $38.99 | -3.1% | 166.3K |
 ANIP | ANI Pharmaceuticals, Inc. | $1.8b | $78.89 | +1.1% | 69.8K |
 NTLA | Intellia Therapeutics, Inc | $1.6b | $12.40 | -9.3% | 5.5M |
 OCS | Oculis Holding AG Ordinary shares | $1.5b | $28.22 | -6.8% | 246.4K |
 AGIO | Agios Pharmaceuticals, Inc. | $1.5b | $28.14 | -0.1% | 212.7K |
 ARDX | Ardelyx, Inc. | $1.5b | $6.08 | -2.3% | 1.8M |
 DMRA | Damora Therapeutics, Inc. Common Stock | $1.5b | $24.57 | -0.1% | 113.9K |