Gene Therapy & Gene Editing

Part of Healthcare - Genomics & Precision Medicine
VRTXVRTXVertex Pharmaceuticals Inc$126.1b$486.51-0.1%776.5K
REGNREGNRegeneron Pharmaceuticals Inc$65.4b$676.50-0.3%479.2K
INSMINSMInsmed, Inc.$23.1b$109.04+0.8%1.7M
BMRNBMRNBioMarin Pharmaceuticals Inc$11.1b$58.50-0.7%1.0M
KRYSKRYSKrystal Biotech, Inc. Common Stock$11.0b$354.52+3.8%263.6K
CRSPCRSPCRISPR Therapeutics AG$5.4b$47.87-1.6%1.4M
FOLDFOLDAmicus Therapeutics, Inc$4.5b$14.49+0.0%3.5M
BEAMBEAMBeam Therapeutics Inc. Common Stock$3.5b$28.14-3.0%1.6M
QUREQUREuniQure N.V.$3.2b$40.65+2.3%853.4K
NTLANTLAIntellia Therapeutics, Inc$2.4b$11.51-4.1%3.8M
VCELVCELVericel Corporation$2.3b$46.63-2.4%375.2K
PGENPGENPrecigen, Inc. Common Stock$2.0b$5.000.0%2.6M
TSHATSHATaysha Gene Therapies, Inc. Common Stock$2.0b$6.12-0.3%2.4M
SRPTSRPTSarepta Therapeutics,, Inc. Common Stock$1.9b$17.30-0.2%2.3M
BLFSBLFSBioLife Solutions Inc.$1.4b$29.14-3.8%1.3M
MGTXMGTXMeiraGTx Holdings plc Ordinary Shares$1.3b$12.44+0.7%369.5K
PCRXPCRXPacira BioSciences, Inc. Common Stock$1.0b$25.61-0.0%295.3K
SLDBSLDBSolid Biosciences Inc. Common Stock$1.0b$9.25-3.8%1.3M
SANASANASana Biotechnology, Inc. Common Stock$1.0b$3.15-1.1%2.3M
DSGNDSGNDesign Therapeutics, Inc. Common Stock$0.9b$12.57-0.2%370.1K
CYRXCYRXCryoPort, Inc. Common Stock$0.8b$16.50+0.1%613.8K
ALLOALLOAllogene Therapeutics, Inc. Common Stock$0.7b$1.80+0.8%4.5M
FDMTFDMT4D Molecular Therapeutics, Inc. Common Stock$0.7b$10.92+1.3%472.7K
PRMEPRMEPrime Medicine, Inc. Common Stock$0.7b$3.22-2.8%2.9M
RGNXRGNXREGENXBIO Inc.$0.6b$9.84-11.9%7.1M
KYTXKYTXKyverna Therapeutics, Inc. Common Stock$0.5b$7.500.0%783.1K
OCGNOCGNOcugen, Inc. Common Stock$0.5b$1.35-0.7%3.5M
CABACABACabaletta Bio, Inc. Common Stock$0.5b$2.83+6.9%3.1M
EDITEDITEditas Medicine, Inc. Common Stock$497.2m$2.97+3.1%1.6M
NGNENGNENeurogene, Inc. Common Stock$497.0m$37.38+2.5%452.5K
BNTCBNTCBenitec Biopharma Inc. Common Stock$459.7m$12.80+1.1%68.4K
RCKTRCKTRocket Pharmaceuticals, Inc. Common Stock$373.4m$3.41+0.6%1.3M
LXEOLXEOLexeo Therapeutics, Inc. Common Stock$365.5m$4.58+2.6%637.3K
ABEOABEOAbeona Therapeutics Inc. Common Stock$352.2m$6.96-0.4%708.0K
IRDIRDOpus Genetics, Inc. Common Stock$339.3m$3.21-0.6%447.8K
TRDATRDAEntrada Therapeutics, Inc. Common Stock$285.7m$6.88-0.1%342.2K
VYGRVYGRVoyager Therapeutics, Inc. Common Stock$211.5m$3.08+4.3%864.7K
DTILDTILPrecision BioSciences, Inc. Common Stock$202.8m$7.86-5.5%254.3K
KRROKRROKorro Bio, Inc. Common Stock$190.1m$12.22-0.2%148.5K
CRBUCRBUCaribou Biosciences, Inc. Common Stock$174.6m$1.69-0.6%1.3M
TNYATNYATenaya Therapeutics, Inc. Common Stock$160.4m$0.80-3.6%1.7M
GNLXGNLXGenelux Corporation Common Stock$135.0m$2.87+1.8%73.8K
MXCTMXCTMaxCyte, Inc. Common Stock$131.8m$1.25-8.1%720.0K
ENGNENGNenGene Therapeutics Inc. Common Stock$115.9m$1.82-4.7%785.8K
CBUSCBUSCibus, Inc. Class A Common Stock$104.6m$1.83-1.1%199.1K
INOINOInovio Pharmaceuticals, Inc.$90.5m$1.130.0%806.0K
SGMOSGMOSangamo Therapeutics, Inc. Common Stock$83.3m$0.18-17.5%6.9M
TCRXTCRXTScan Therapeutics, Inc. Common Stock$64.1m$0.92+1.4%140.8K
TILTILInstil Bio, Inc. Common Stock$52.2m$7.43-0.8%8.5K
MGXMGXMetagenomi Therapeutics, Inc. Common Stock$44.8m$1.24-0.4%126.2K

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