VRTX | Vertex Pharmaceuticals Inc | $112.6b | $430.24 | -1.1% | 1.1M |
REGN | Regeneron Pharmaceuticals Inc | $79.2b | $751.48 | -1.9% | 809.5K |
INSM | Insmed, Inc. | $33.0b | $135.16 | -6.0% | 2.5M |
BMRN | BioMarin Pharmaceuticals Inc | $10.5b | $53.16 | -1.5% | 1.1M |
KRYS | Krystal Biotech, Inc. Common Stock | $7.2b | $272.51 | +1.7% | 264.1K |
FOLD | Amicus Therapeutics, Inc | $4.5b | $14.49 | +0.2% | 5.3M |
CRSP | CRISPR Therapeutics AG | $4.3b | $48.79 | -11.6% | 3.9M |
BEAM | Beam Therapeutics Inc. Common Stock | $2.2b | $27.11 | -10.1% | 4.7M |
SRPT | Sarepta Therapeutics,, Inc. Common Stock | $2.2b | $20.27 | -0.7% | 2.1M |
VCEL | Vericel Corporation | $1.6b | $35.61 | +3.5% | 565.7K |
NTLA | Intellia Therapeutics, Inc | $1.4b | $16.00 | +0.8% | 9.0M |
TSHA | Taysha Gene Therapies, Inc. Common Stock | $1.2b | $6.39 | -0.2% | 1.9M |
PGEN | Precigen, Inc. Common Stock | $1.2b | $4.13 | +4.2% | 3.5M |
PCRX | Pacira BioSciences, Inc. Common Stock | $0.9b | $24.51 | -3.4% | 525.9K |
QURE | uniQure N.V. | $0.9b | $18.06 | +3.0% | 1.0M |
BLFS | BioLife Solutions Inc. | $0.9b | $21.36 | -1.7% | 362.4K |
SANA | Sana Biotechnology, Inc. Common Stock | $0.7b | $3.29 | -4.5% | 2.7M |
MGTX | MeiraGTx Holdings plc Ordinary Shares | $0.7b | $9.22 | -1.1% | 673.4K |
DSGN | Design Therapeutics, Inc. Common Stock | $0.6b | $12.54 | -1.9% | 413.2K |
SLDB | Solid Biosciences Inc. Common Stock | $0.6b | $7.90 | -3.9% | 737.0K |
OCGN | Ocugen, Inc. Common Stock | $0.6b | $1.67 | 0.0% | 6.1M |
PRME | Prime Medicine, Inc. Common Stock | $0.6b | $3.70 | -3.6% | 1.6M |
ALLO | Allogene Therapeutics, Inc. Common Stock | $0.5b | $2.29 | -2.5% | 5.5M |
KYTX | Kyverna Therapeutics, Inc. Common Stock | $458.3m | $9.05 | +1.2% | 1.5M |
TRDA | Entrada Therapeutics, Inc. Common Stock | $450.6m | $12.64 | -1.3% | 161.0K |
FDMT | 4D Molecular Therapeutics, Inc. Common Stock | $437.5m | $9.42 | -2.0% | 514.6K |
ENGN | enGene Holdings Inc. Common Stock | $414.0m | $8.00 | -1.7% | 222.2K |
RGNX | REGENXBIO Inc. | $401.0m | $8.78 | -2.3% | 757.0K |
CYRX | CryoPort, Inc. Common Stock | $393.4m | $10.59 | +4.1% | 243.9K |
LXEO | Lexeo Therapeutics, Inc. Common Stock | $384.6m | $5.86 | -2.5% | 940.5K |
RCKT | Rocket Pharmaceuticals, Inc. Common Stock | $374.0m | $3.53 | -4.1% | 1.9M |
BNTC | Benitec Biopharma Inc. Common Stock | $344.6m | $12.37 | -2.6% | 140.9K |
IRD | Opus Genetics, Inc. Common Stock | $309.5m | $5.22 | +0.2% | 655.5K |
NGNE | Neurogene, Inc. Common Stock | $300.6m | $27.03 | +0.3% | 273.1K |
CABA | Cabaletta Bio, Inc. Common Stock | $275.0m | $2.94 | -3.6% | 2.0M |
ABEO | Abeona Therapeutics Inc. Common Stock | $241.3m | $5.41 | -2.0% | 928.6K |
VYGR | Voyager Therapeutics, Inc. Common Stock | $230.6m | $3.79 | -6.2% | 583.5K |
EDIT | Editas Medicine, Inc. Common Stock | $218.3m | $2.90 | -9.5% | 1.5M |
CRBU | Caribou Biosciences, Inc. Common Stock | $166.2m | $2.13 | -5.8% | 1.9M |
KRRO | Korro Bio, Inc. Common Stock | $148.3m | $12.84 | -5.5% | 100.2K |
CBUS | Cibus, Inc. Class A Common Stock | $138.6m | $1.50 | +3.4% | 396.8K |
TNYA | Tenaya Therapeutics, Inc. Common Stock | $134.5m | $0.67 | -1.4% | 3.2M |
DTIL | Precision BioSciences, Inc. Common Stock | $134.0m | $7.06 | -3.4% | 209.9K |
INO | Inovio Pharmaceuticals, Inc. | $115.4m | $1.14 | 0.0% | 721.5K |
SGMO | Sangamo Therapeutics, Inc. Common Stock | $114.2m | $0.19 | -25.7% | 31.1M |
GNLX | Genelux Corporation Common Stock | $103.1m | $2.54 | +0.6% | 129.5K |
MXCT | MaxCyte, Inc. Common Stock | $72.3m | $0.86 | -0.1% | 343.1K |
TIL | Instil Bio, Inc. Common Stock | $54.1m | $8.05 | -1.6% | 23.7K |
TCRX | TScan Therapeutics, Inc. Common Stock | $53.5m | $1.25 | +4.2% | 1.1M |
MGX | Metagenomi Therapeutics, Inc. Common Stock | $47.6m | $1.50 | +4.9% | 136.8K |