Gene Therapy & Gene Editing

Part of Healthcare - Genomics & Precision Medicine
VRTXVRTXVertex Pharmaceuticals Inc$127.9b$517.46-1.2%940.8K
REGNREGNRegeneron Pharmaceuticals Inc$75.7b$809.64+0.4%322.4K
INSMINSMInsmed, Inc.$24.3b$94.06-0.0%3.0M
BMRNBMRNBioMarin Pharmaceuticals Inc$11.1b$56.00-0.4%1.9M
KRYSKRYSKrystal Biotech, Inc. Common Stock$9.5b$312.94+0.7%182.3K
CRSPCRSPCRISPR Therapeutics AG$5.4b$48.98-0.8%850.2K
FOLDFOLDAmicus Therapeutics, Inc$4.5b$14.49+0.0%3.5M
PGENPGENPrecigen, Inc. Common Stock$3.1b$6.05-2.3%2.1M
BEAMBEAMBeam Therapeutics Inc. Common Stock$2.5b$23.78-1.0%746.9K
VCELVCELVericel Corporation$2.1b$43.03+1.1%551.5K
SRPTSRPTSarepta Therapeutics,, Inc. Common Stock$1.8b$17.75+1.5%1.0M
BLFSBLFSBioLife Solutions Inc.$1.8b$38.600.0%N/A
NTLANTLAIntellia Therapeutics, Inc$1.7b$11.28+0.4%1.6M
QUREQUREuniQure N.V.$1.6b$21.83-3.5%894.2K
TSHATSHATaysha Gene Therapies, Inc. Common Stock$1.5b$4.05+1.0%1.4M
MGTXMGTXMeiraGTx Holdings plc Ordinary Shares$1.0b$9.19-0.4%514.9K
PCRXPCRXPacira BioSciences, Inc. Common Stock$1.0b$36.82-0.1%315.9K
CYRXCYRXCryoPort, Inc. Common Stock$0.9b$17.80-1.1%338.9K
SANASANASana Biotechnology, Inc. Common Stock$0.9b$2.34+1.3%1.3M
DSGNDSGNDesign Therapeutics, Inc. Common Stock$0.8b$10.33+0.8%258.1K
FDMTFDMT4D Molecular Therapeutics, Inc. Common Stock$0.8b$11.04+2.2%962.2K
SLDBSLDBSolid Biosciences Inc. Common Stock$0.7b$5.82-1.7%771.6K
PRMEPRMEPrime Medicine, Inc. Common Stock$0.5b$3.62-1.5%2.3M
ALLOALLOAllogene Therapeutics, Inc. Common Stock$0.5b$1.22-2.4%10.2M
NGNENGNENeurogene, Inc. Common Stock$0.5b$23.57+0.1%102.1K
RGNXRGNXREGENXBIO Inc.$490.5m$6.58-1.6%992.8K
EDITEDITEditas Medicine, Inc. Common Stock$402.4m$2.40+0.4%1.2M
KYTXKYTXKyverna Therapeutics, Inc. Common Stock$384.7m$5.25-2.4%721.4K
IRDIRDOpus Genetics, Inc. Common Stock$381.0m$3.34-4.3%1.4M
OCGNOCGNOcugen, Inc. Common Stock$345.9m$0.71-3.1%7.9M
CABACABACabaletta Bio, Inc. Common Stock$339.1m$1.38-8.8%5.8M
BNTCBNTCBenitec Biopharma Inc. Common Stock$313.2m$8.60-0.8%79.2K
LXEOLXEOLexeo Therapeutics, Inc. Common Stock$289.8m$2.71-3.2%990.8K
ABEOABEOAbeona Therapeutics Inc. Common Stock$287.6m$4.36-1.8%354.0K
RCKTRCKTRocket Pharmaceuticals, Inc. Common Stock$281.0m$2.27-0.7%1.4M
TRDATRDAEntrada Therapeutics, Inc. Common Stock$209.5m$4.75+7.5%551.8K
DTILDTILPrecision BioSciences, Inc. Common Stock$174.2m$6.40-3.5%242.1K
VYGRVYGRVoyager Therapeutics, Inc. Common Stock$151.0m$1.77+0.9%1.5M
KRROKRROKorro Bio, Inc. Common Stock$142.0m$13.14+0.7%163.8K
CRBUCRBUCaribou Biosciences, Inc. Common Stock$130.8m$0.52-7.7%1.9M
CBUSCBUSCibus, Inc. Class A Common Stock$130.7m$1.39-0.7%49.9K
ENGNENGNenGene Therapeutics Inc. Common Stock$130.0m$1.57+1.3%653.1K
TNYATNYATenaya Therapeutics, Inc. Common Stock$126.5m$0.41+5.4%3.4M
INOINOInovio Pharmaceuticals, Inc.$119.9m$0.89-2.8%2.8M
GNLXGNLXGenelux Corporation Common Stock$115.8m$1.94-4.5%490.4K
MXCTMXCTMaxCyte, Inc. Common Stock$110.4m$1.49+8.6%1.1M
SGMOSGMOSangamo Therapeutics, Inc. Common Stock$83.3m$0.18-17.5%6.9M
GRMLGRMLGreenland Mines Ltd. Common Stock$60.0m$5.72+0.5%609.4K
TILTILInstil Bio, Inc. Common Stock$49.0m$5.67-0.8%36.3K
MGXMGXMetagenomi Therapeutics, Inc. Common Stock$38.5m$0.76-4.1%208.5K

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