Gene Therapy & Gene Editing

Part of Healthcare - Genomics & Precision Medicine
VRTXVRTXVertex Pharmaceuticals Inc$119.5b$545.52-1.0%556.1K
REGNREGNRegeneron Pharmaceuticals Inc$78.2b$812.58-2.2%291.5K
INSMINSMInsmed, Inc.$21.4b$125.08+0.4%1.1M
BMRNBMRNBioMarin Pharmaceuticals Inc$11.6b$65.74-0.8%1.4M
KRYSKRYSKrystal Biotech, Inc. Common Stock$10.1b$358.50+1.1%246.3K
CRSPCRSPCRISPR Therapeutics AG$4.7b$59.41-2.7%837.6K
FOLDFOLDAmicus Therapeutics, Inc$4.5b$14.49+0.0%3.5M
QUREQUREuniQure N.V.$3.1b$50.46-0.2%823.2K
BEAMBEAMBeam Therapeutics Inc. Common Stock$2.6b$30.41-2.6%1.0M
VCELVCELVericel Corporation$2.4b$42.44-1.9%248.7K
PGENPGENPrecigen, Inc. Common Stock$2.4b$7.59+1.6%6.8M
SRPTSRPTSarepta Therapeutics,, Inc. Common Stock$1.7b$19.36+2.9%2.1M
TSHATSHATaysha Gene Therapies, Inc. Common Stock$1.7b$6.12-3.1%1.1M
BLFSBLFSBioLife Solutions Inc.$1.5b$37.12-0.6%787.1K
NTLANTLAIntellia Therapeutics, Inc$1.5b$13.40-2.4%2.4M
MGTXMGTXMeiraGTx Holdings plc Ordinary Shares$1.1b$14.55-2.4%535.7K
PCRXPCRXPacira BioSciences, Inc. Common Stock$1.1b$25.91+1.6%432.4K
SANASANASana Biotechnology, Inc. Common Stock$0.9b$4.17+1.5%2.1M
SLDBSLDBSolid Biosciences Inc. Common Stock$0.8b$9.73-1.5%497.7K
DSGNDSGNDesign Therapeutics, Inc. Common Stock$0.8b$15.58-0.7%670.2K
CYRXCYRXCryoPort, Inc. Common Stock$0.8b$16.57-0.9%220.6K
NGNENGNENeurogene, Inc. Common Stock$0.7b$38.34-4.9%158.3K
ALLOALLOAllogene Therapeutics, Inc. Common Stock$0.6b$2.04-6.5%4.7M
RGNXRGNXREGENXBIO Inc.$0.6b$9.24+5.4%963.4K
FDMTFDMT4D Molecular Therapeutics, Inc. Common Stock$0.5b$15.74-1.1%620.8K
PRMEPRMEPrime Medicine, Inc. Common Stock$0.5b$3.45-3.5%1.7M
KYTXKYTXKyverna Therapeutics, Inc. Common Stock$443.8m$8.61-2.4%380.6K
CABACABACabaletta Bio, Inc. Common Stock$437.0m$3.21+1.2%2.2M
OCGNOCGNOcugen, Inc. Common Stock$423.9m$1.41+1.4%1.7M
BNTCBNTCBenitec Biopharma Inc. Common Stock$402.3m$12.87-0.9%50.9K
EDITEDITEditas Medicine, Inc. Common Stock$395.9m$3.21-3.4%2.7M
RCKTRCKTRocket Pharmaceuticals, Inc. Common Stock$372.4m$3.73-2.9%1.1M
ABEOABEOAbeona Therapeutics Inc. Common Stock$365.9m$6.09-3.2%1.1M
LXEOLXEOLexeo Therapeutics, Inc. Common Stock$324.3m$5.00-2.4%584.4K
IRDIRDOpus Genetics, Inc. Common Stock$306.3m$3.79-7.8%837.5K
TRDATRDAEntrada Therapeutics, Inc. Common Stock$281.8m$7.13-7.6%198.7K
VYGRVYGRVoyager Therapeutics, Inc. Common Stock$181.3m$3.44-0.7%246.9K
DTILDTILPrecision BioSciences, Inc. Common Stock$180.4m$8.68-0.8%240.2K
TNYATNYATenaya Therapeutics, Inc. Common Stock$158.2m$0.70-0.2%903.2K
KRROKRROKorro Bio, Inc. Common Stock$149.6m$13.66+0.9%34.5K
CBUSCBUSCibus, Inc. Class A Common Stock$147.3m$1.69-0.6%85.8K
CRBUCRBUCaribou Biosciences, Inc. Common Stock$144.8m$1.66-6.5%788.6K
GNLXGNLXGenelux Corporation Common Stock$131.8m$2.74+0.4%263.8K
ENGNENGNenGene Therapeutics Inc. Common Stock$119.9m$1.90+4.3%1.8M
MXCTMXCTMaxCyte, Inc. Common Stock$114.6m$1.33-3.0%281.7K
SGMOSGMOSangamo Therapeutics, Inc. Common Stock$83.3m$0.18-17.5%6.9M
INOINOInovio Pharmaceuticals, Inc.$55.7m$1.28+1.2%3.7M
TILTILInstil Bio, Inc. Common Stock$49.0m$7.820.0%10.5K
TCRXTCRXTScan Therapeutics, Inc. Common Stock$47.3m$0.78-2.1%66.1K
MGXMGXMetagenomi Therapeutics, Inc. Common Stock$45.6m$1.22+0.8%58.9K

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