Gene Therapy & Gene Editing

Part of Healthcare - Genomics & Precision Medicine
VRTXVRTXVertex Pharmaceuticals Inc$141.4b$515.280.0%19
REGNREGNRegeneron Pharmaceuticals Inc$86.8b$773.080.0%51
INSMINSMInsmed, Inc.$27.7b$120.980.0%263
BMRNBMRNBioMarin Pharmaceuticals Inc$13.0b$64.570.0%117
KRYSKRYSKrystal Biotech, Inc. Common Stock$10.9b$336.600.0%357
CRSPCRSPCRISPR Therapeutics AG$5.5b$52.420.0%3.8K
FOLDFOLDAmicus Therapeutics, Inc$4.5b$14.49+0.0%3.5M
QUREQUREuniQure N.V.$3.1b$43.240.0%55.7K
BEAMBEAMBeam Therapeutics Inc. Common Stock$3.0b$23.380.0%2.8K
PGENPGENPrecigen, Inc. Common Stock$2.6b$6.950.0%2
SRPTSRPTSarepta Therapeutics,, Inc. Common Stock$2.4b$21.360.0%78
VCELVCELVericel Corporation$2.1b$39.750.0%631
TSHATSHATaysha Gene Therapies, Inc. Common Stock$1.8b$5.040.0%19
NTLANTLAIntellia Therapeutics, Inc$1.8b$11.430.0%4.2K
BLFSBLFSBioLife Solutions Inc.$1.8b$36.510.0%N/A
MGTXMGTXMeiraGTx Holdings plc Ordinary Shares$1.3b$12.940.0%108
SANASANASana Biotechnology, Inc. Common Stock$1.2b$3.170.0%3.3K
SLDBSLDBSolid Biosciences Inc. Common Stock$1.1b$8.370.0%201
PCRXPCRXPacira BioSciences, Inc. Common Stock$1.1b$24.100.0%1.9K
DSGNDSGNDesign Therapeutics, Inc. Common Stock$1.0b$12.230.0%N/A
FDMTFDMT4D Molecular Therapeutics, Inc. Common Stock$0.8b$13.750.0%360
CYRXCYRXCryoPort, Inc. Common Stock$0.8b$16.370.0%275
NGNENGNENeurogene, Inc. Common Stock$0.8b$33.670.0%N/A
ALLOALLOAllogene Therapeutics, Inc. Common Stock$0.7b$1.740.0%284
PRMEPRMEPrime Medicine, Inc. Common Stock$0.7b$3.170.0%44
RGNXRGNXREGENXBIO Inc.$0.6b$7.890.0%180
CABACABACabaletta Bio, Inc. Common Stock$0.6b$2.580.0%2.4K
KYTXKYTXKyverna Therapeutics, Inc. Common Stock$0.5b$6.980.0%N/A
EDITEDITEditas Medicine, Inc. Common Stock$473.0m$2.750.0%23
OCGNOCGNOcugen, Inc. Common Stock$457.8m$1.000.0%1.7K
BNTCBNTCBenitec Biopharma Inc. Common Stock$442.5m$11.050.0%N/A
RCKTRCKTRocket Pharmaceuticals, Inc. Common Stock$416.0m$3.670.0%14.3K
LXEOLXEOLexeo Therapeutics, Inc. Common Stock$392.2m$4.130.0%1
IRDIRDOpus Genetics, Inc. Common Stock$370.2m$5.890.0%1.8K
ABEOABEOAbeona Therapeutics Inc. Common Stock$340.2m$5.510.0%N/A
TRDATRDAEntrada Therapeutics, Inc. Common Stock$279.2m$6.720.0%N/A
VYGRVYGRVoyager Therapeutics, Inc. Common Stock$208.3m$3.100.0%1
DTILDTILPrecision BioSciences, Inc. Common Stock$205.6m$6.620.0%28
KRROKRROKorro Bio, Inc. Common Stock$176.3m$14.350.0%N/A
CRBUCRBUCaribou Biosciences, Inc. Common Stock$171.5m$1.290.0%780
TNYATNYATenaya Therapeutics, Inc. Common Stock$155.9m$0.680.0%351
INOINOInovio Pharmaceuticals, Inc.$140.6m$1.170.0%421
MXCTMXCTMaxCyte, Inc. Common Stock$130.0m$1.180.0%N/A
ENGNENGNenGene Therapeutics Inc. Common Stock$126.6m$1.900.0%668
CBUSCBUSCibus, Inc. Class A Common Stock$119.2m$1.570.0%N/A
GNLXGNLXGenelux Corporation Common Stock$115.4m$2.500.0%8
SGMOSGMOSangamo Therapeutics, Inc. Common Stock$83.3m$0.18-17.5%6.9M
TILTILInstil Bio, Inc. Common Stock$51.9m$7.220.0%N/A
MGXMGXMetagenomi Therapeutics, Inc. Common Stock$43.8m$1.180.0%N/A
TCRXTCRXTScan Therapeutics, Inc. Common Stock$25.1m$0.330.0%2.5K

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