Gene Therapy & Gene Editing

Part of Healthcare - Genomics & Precision Medicine
VRTXVRTXVertex Pharmaceuticals Inc$119.5b$486.56-0.2%731.4K
REGNREGNRegeneron Pharmaceuticals Inc$78.2b$767.67+0.4%327.6K
INSMINSMInsmed, Inc.$21.4b$131.92+33.9%11.3M
BMRNBMRNBioMarin Pharmaceuticals Inc$11.6b$64.42+2.6%2.8M
KRYSKRYSKrystal Biotech, Inc. Common Stock$10.1b$322.25-0.9%140.1K
CRSPCRSPCRISPR Therapeutics AG$4.7b$51.64-1.6%836.3K
FOLDFOLDAmicus Therapeutics, Inc$4.5b$14.49+0.0%3.5M
QUREQUREuniQure N.V.$3.1b$46.79+2.7%1.1M
BEAMBEAMBeam Therapeutics Inc. Common Stock$2.6b$27.45+0.6%964.0K
VCELVCELVericel Corporation$2.4b$44.73-1.3%255.8K
PGENPGENPrecigen, Inc. Common Stock$2.4b$6.99+0.1%6.1M
SRPTSRPTSarepta Therapeutics,, Inc. Common Stock$1.7b$16.77+5.3%3.7M
TSHATSHATaysha Gene Therapies, Inc. Common Stock$1.7b$6.40-1.9%1.7M
BLFSBLFSBioLife Solutions Inc.$1.5b$33.15+0.3%382.4K
NTLANTLAIntellia Therapeutics, Inc$1.5b$11.58+2.5%3.8M
MGTXMGTXMeiraGTx Holdings plc Ordinary Shares$1.1b$12.80+2.0%268.7K
PCRXPCRXPacira BioSciences, Inc. Common Stock$1.1b$26.38+2.9%733.3K
SANASANASana Biotechnology, Inc. Common Stock$0.9b$3.37-2.8%1.5M
SLDBSLDBSolid Biosciences Inc. Common Stock$0.8b$8.13-0.3%483.7K
DSGNDSGNDesign Therapeutics, Inc. Common Stock$0.8b$14.07+1.5%291.5K
CYRXCYRXCryoPort, Inc. Common Stock$0.8b$15.39-3.7%560.7K
NGNENGNENeurogene, Inc. Common Stock$0.7b$35.59-1.3%75.9K
ALLOALLOAllogene Therapeutics, Inc. Common Stock$0.6b$1.97+1.0%2.9M
RGNXRGNXREGENXBIO Inc.$0.6b$11.43+7.4%1.6M
FDMTFDMT4D Molecular Therapeutics, Inc. Common Stock$0.5b$10.65+2.8%225.9K
PRMEPRMEPrime Medicine, Inc. Common Stock$0.5b$2.93-5.0%2.2M
KYTXKYTXKyverna Therapeutics, Inc. Common Stock$443.8m$7.76+1.6%447.3K
CABACABACabaletta Bio, Inc. Common Stock$437.0m$2.75+2.2%2.5M
OCGNOCGNOcugen, Inc. Common Stock$423.9m$1.25-2.3%5.1M
BNTCBNTCBenitec Biopharma Inc. Common Stock$402.3m$13.14+3.9%49.7K
EDITEDITEditas Medicine, Inc. Common Stock$395.9m$2.88+5.6%3.2M
RCKTRCKTRocket Pharmaceuticals, Inc. Common Stock$372.4m$3.56+0.9%1.9M
ABEOABEOAbeona Therapeutics Inc. Common Stock$365.9m$6.93+1.5%773.1K
LXEOLXEOLexeo Therapeutics, Inc. Common Stock$324.3m$4.54+2.2%1.3M
IRDIRDOpus Genetics, Inc. Common Stock$306.3m$3.73-1.6%572.0K
TRDATRDAEntrada Therapeutics, Inc. Common Stock$281.8m$7.03-2.5%234.4K
VYGRVYGRVoyager Therapeutics, Inc. Common Stock$181.3m$3.13+0.6%367.7K
DTILDTILPrecision BioSciences, Inc. Common Stock$180.4m$7.42-0.7%235.1K
TNYATNYATenaya Therapeutics, Inc. Common Stock$158.2m$0.75-7.5%2.9M
KRROKRROKorro Bio, Inc. Common Stock$149.6m$12.13+5.9%131.3K
CBUSCBUSCibus, Inc. Class A Common Stock$147.3m$1.92-4.1%102.1K
CRBUCRBUCaribou Biosciences, Inc. Common Stock$144.8m$1.63+1.9%788.7K
GNLXGNLXGenelux Corporation Common Stock$131.8m$2.75+7.2%196.9K
ENGNENGNenGene Therapeutics Inc. Common Stock$119.9m$1.790.0%292.5K
MXCTMXCTMaxCyte, Inc. Common Stock$114.6m$1.11+4.2%846.9K
SGMOSGMOSangamo Therapeutics, Inc. Common Stock$83.3m$0.18-17.5%6.9M
INOINOInovio Pharmaceuticals, Inc.$55.7m$0.67-1.6%1.7M
TILTILInstil Bio, Inc. Common Stock$49.0m$7.390.0%2.0K
TCRXTCRXTScan Therapeutics, Inc. Common Stock$47.3m$0.78-1.8%126.0K
MGXMGXMetagenomi Therapeutics, Inc. Common Stock$45.6m$1.23+1.2%144.7K

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