Gene Therapy & Gene Editing

Part of Healthcare - Genomics & Precision Medicine
VRTXVRTXVertex Pharmaceuticals Inc$127.9b$501.99-0.2%475.7K
REGNREGNRegeneron Pharmaceuticals Inc$75.7b$734.30+1.6%411.6K
INSMINSMInsmed, Inc.$24.3b$104.95+1.3%3.1M
BMRNBMRNBioMarin Pharmaceuticals Inc$11.1b$56.23-2.3%2.5M
KRYSKRYSKrystal Biotech, Inc. Common Stock$9.5b$330.83-2.3%299.9K
CRSPCRSPCRISPR Therapeutics AG$5.4b$54.16-5.9%2.4M
FOLDFOLDAmicus Therapeutics, Inc$4.5b$14.49+0.0%3.5M
PGENPGENPrecigen, Inc. Common Stock$3.1b$7.58-2.5%4.7M
BEAMBEAMBeam Therapeutics Inc. Common Stock$2.5b$25.52-1.7%2.2M
VCELVCELVericel Corporation$2.1b$40.03-2.5%576.0K
SRPTSRPTSarepta Therapeutics,, Inc. Common Stock$1.8b$17.32-1.0%1.9M
BLFSBLFSBioLife Solutions Inc.$1.8b$38.600.0%N/A
NTLANTLAIntellia Therapeutics, Inc$1.7b$12.40-3.0%7.3M
QUREQUREuniQure N.V.$1.6b$23.14+1.1%2.5M
TSHATSHATaysha Gene Therapies, Inc. Common Stock$1.5b$4.58-2.2%2.7M
MGTXMGTXMeiraGTx Holdings plc Ordinary Shares$1.0b$10.60-3.1%774.3K
PCRXPCRXPacira BioSciences, Inc. Common Stock$1.0b$24.77-1.2%349.1K
CYRXCYRXCryoPort, Inc. Common Stock$0.9b$17.66-1.8%687.4K
SANASANASana Biotechnology, Inc. Common Stock$0.9b$2.81-4.2%3.4M
DSGNDSGNDesign Therapeutics, Inc. Common Stock$0.8b$11.96-3.3%568.2K
FDMTFDMT4D Molecular Therapeutics, Inc. Common Stock$0.8b$12.64-2.8%914.9K
SLDBSLDBSolid Biosciences Inc. Common Stock$0.7b$6.92-2.0%978.1K
PRMEPRMEPrime Medicine, Inc. Common Stock$0.5b$3.55+9.0%11.6M
ALLOALLOAllogene Therapeutics, Inc. Common Stock$0.5b$1.46-3.0%4.4M
NGNENGNENeurogene, Inc. Common Stock$0.5b$25.45-3.7%102.0K
RGNXRGNXREGENXBIO Inc.$490.5m$7.63-3.9%1.0M
EDITEDITEditas Medicine, Inc. Common Stock$402.4m$2.74-2.3%2.8M
KYTXKYTXKyverna Therapeutics, Inc. Common Stock$384.7m$6.22-2.5%670.3K
IRDIRDOpus Genetics, Inc. Common Stock$381.0m$4.41+0.3%2.4M
OCGNOCGNOcugen, Inc. Common Stock$345.9m$1.05+0.5%4.9M
CABACABACabaletta Bio, Inc. Common Stock$339.1m$2.02-2.6%3.6M
BNTCBNTCBenitec Biopharma Inc. Common Stock$313.2m$9.00-2.5%199.2K
LXEOLXEOLexeo Therapeutics, Inc. Common Stock$289.8m$3.31-2.6%1.4M
ABEOABEOAbeona Therapeutics Inc. Common Stock$287.6m$5.06-1.8%1.2M
RCKTRCKTRocket Pharmaceuticals, Inc. Common Stock$281.0m$2.50-5.0%1.6M
TRDATRDAEntrada Therapeutics, Inc. Common Stock$209.5m$5.42-1.1%266.8K
DTILDTILPrecision BioSciences, Inc. Common Stock$174.2m$6.21-1.9%174.1K
VYGRVYGRVoyager Therapeutics, Inc. Common Stock$151.0m$2.47-0.2%560.5K
KRROKRROKorro Bio, Inc. Common Stock$142.0m$9.77-2.0%129.0K
CRBUCRBUCaribou Biosciences, Inc. Common Stock$130.8m$0.66-4.6%1.0M
CBUSCBUSCibus, Inc. Class A Common Stock$130.7m$1.58-5.4%160.4K
ENGNENGNenGene Therapeutics Inc. Common Stock$130.0m$1.80-3.5%348.8K
TNYATNYATenaya Therapeutics, Inc. Common Stock$126.5m$0.56-2.9%2.6M
INOINOInovio Pharmaceuticals, Inc.$119.9m$1.14-2.6%2.0M
GNLXGNLXGenelux Corporation Common Stock$115.8m$2.54-2.3%76.5K
MXCTMXCTMaxCyte, Inc. Common Stock$110.4m$1.05+0.9%317.8K
SGMOSGMOSangamo Therapeutics, Inc. Common Stock$83.3m$0.18-17.5%6.9M
GRMLGRMLGreenland Mines Ltd. Common Stock$60.0m$6.42-13.8%4.7M
TILTILInstil Bio, Inc. Common Stock$49.0m$6.89-0.9%24.0K
MGXMGXMetagenomi Therapeutics, Inc. Common Stock$38.5m$1.03-0.5%119.6K

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