Gene Therapy & Gene Editing

Part of Healthcare - Genomics & Precision Medicine
VRTXVRTXVertex Pharmaceuticals Inc$113.6b$489.29+2.3%3.0M
REGNREGNRegeneron Pharmaceuticals Inc$64.5b$629.25+2.1%689.1K
INSMINSMInsmed, Inc.$23.2b$104.75-0.9%3.4M
BMRNBMRNBioMarin Pharmaceuticals Inc$11.1b$59.30+2.9%1.9M
KRYSKRYSKrystal Biotech, Inc. Common Stock$9.1b$366.76+3.3%464.7K
CRSPCRSPCRISPR Therapeutics AG$5.4b$54.52+1.7%1.7M
FOLDFOLDAmicus Therapeutics, Inc$4.5b$14.49+0.0%3.5M
BEAMBEAMBeam Therapeutics Inc. Common Stock$3.4b$35.19+2.6%2.6M
NTLANTLAIntellia Therapeutics, Inc$2.0b$16.63+3.9%4.4M
SRPTSRPTSarepta Therapeutics,, Inc. Common Stock$1.9b$16.90+5.2%3.8M
QUREQUREuniQure N.V.$1.8b$47.66-3.1%2.8M
VCELVCELVericel Corporation$1.7b$46.26+7.7%1.2M
TSHATSHATaysha Gene Therapies, Inc. Common Stock$1.7b$6.28+2.3%3.7M
PGENPGENPrecigen, Inc. Common Stock$1.5b$5.82+6.2%5.8M
BLFSBLFSBioLife Solutions Inc.$1.2b$29.75+4.2%2.4M
MGTXMGTXMeiraGTx Holdings plc Ordinary Shares$1.0b$12.10+4.7%884.2K
SANASANASana Biotechnology, Inc. Common Stock$0.9b$3.44+4.6%3.1M
PCRXPCRXPacira BioSciences, Inc. Common Stock$0.9b$25.25+3.4%502.5K
CYRXCYRXCryoPort, Inc. Common Stock$0.8b$15.97+0.9%559.4K
ALLOALLOAllogene Therapeutics, Inc. Common Stock$0.7b$2.13+2.9%7.6M
SLDBSLDBSolid Biosciences Inc. Common Stock$0.7b$9.12+4.6%1.6M
DSGNDSGNDesign Therapeutics, Inc. Common Stock$0.7b$13.36-1.0%788.7K
PRMEPRMEPrime Medicine, Inc. Common Stock$0.6b$3.44+7.9%4.1M
CABACABACabaletta Bio, Inc. Common Stock$0.6b$3.03+3.8%7.4M
EDITEDITEditas Medicine, Inc. Common Stock$0.5b$2.79+4.4%2.0M
FDMTFDMT4D Molecular Therapeutics, Inc. Common Stock$0.5b$11.36+0.9%1.1M
KYTXKYTXKyverna Therapeutics, Inc. Common Stock$0.5b$8.29+3.0%822.2K
OCGNOCGNOcugen, Inc. Common Stock$467.2m$1.50+8.4%12.4M
NGNENGNENeurogene, Inc. Common Stock$447.8m$32.03+5.4%317.7K
LXEOLXEOLexeo Therapeutics, Inc. Common Stock$403.6m$4.76+1.4%506.4K
BNTCBNTCBenitec Biopharma Inc. Common Stock$397.1m$12.37-4.2%229.0K
RGNXRGNXREGENXBIO Inc.$362.4m$10.46+2.7%2.0M
IRDIRDOpus Genetics, Inc. Common Stock$354.9m$4.02+7.5%1.4M
RCKTRCKTRocket Pharmaceuticals, Inc. Common Stock$335.2m$3.270.0%3.3M
ABEOABEOAbeona Therapeutics Inc. Common Stock$329.4m$5.62+1.1%1.4M
TRDATRDAEntrada Therapeutics, Inc. Common Stock$274.5m$7.74+8.0%665.2K
CRBUCRBUCaribou Biosciences, Inc. Common Stock$234.1m$1.67+6.4%2.0M
VYGRVYGRVoyager Therapeutics, Inc. Common Stock$233.8m$3.58+0.8%821.2K
KRROKRROKorro Bio, Inc. Common Stock$193.4m$12.66+4.1%164.1K
TNYATNYATenaya Therapeutics, Inc. Common Stock$188.6m$0.72+1.1%1.2M
DTILDTILPrecision BioSciences, Inc. Common Stock$179.8m$7.26+8.4%482.9K
GNLXGNLXGenelux Corporation Common Stock$136.8m$3.23-1.0%303.6K
MXCTMXCTMaxCyte, Inc. Common Stock$129.6m$1.21-1.6%2.0M
ENGNENGNenGene Therapeutics Inc. Common Stock$123.9m$1.75-1.1%1.2M
CBUSCBUSCibus, Inc. Class A Common Stock$109.9m$1.350.0%204.4K
INOINOInovio Pharmaceuticals, Inc.$107.8m$1.10+0.9%1.1M
SGMOSGMOSangamo Therapeutics, Inc. Common Stock$83.3m$0.18-17.5%6.9M
TCRXTCRXTScan Therapeutics, Inc. Common Stock$70.6m$0.91+14.7%651.5K
TILTILInstil Bio, Inc. Common Stock$54.7m$7.440.0%14.9K
MGXMGXMetagenomi Therapeutics, Inc. Common Stock$51.2m$1.25+5.0%178.5K

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